2026 TUBB4A Virtual Family Conference

Philadelphia, PA - The Leukodystrophy Center at the Children’s Hospital of Philadelphia was honored to host the 2026 TUBB4A Virtual Family Conference on Saturday, May 23, 2026. This featured featured presentation by some of the world’s leading clinicians and scientists for TUBB4A-related leukodystrophy, along with biotechnology and pharmaceutical companies working to develop therapies, and advocacy leaders working to raise awareness and funding for tomorrow’s discoveries. 

Thanks to the support of our audiovisual partners at Lafayette Hill Studios, high-quality video recordings of each session are now available for review via the links below. We would also like to extend a huge ‘THANK YOU’ to the Foundation to Fight H-ABC for co-sponsoring this event and working closely with us and the other advocacy leaders in this space - including Fundación Leucodistrofia TUBB4A, H-ABC Foundation UK, Kinslow TUBB4A Foundation - to develop the event agenda.

If you have any questions regarding the meeting or are interested in engaging with us, please contact Omar Sherbini (CHOP Leukodystrophy Center Administrative Director) sherbinio@chop.edu.

Session 1 - introduction

Session II - clinical research

Session III - preclinical work

Session IV - Therapeutic Development

Session V - Advocacy Showcase